Thank You! A message of hope from BGF’s Board of Directors
We are making big advances in offering hope, and we couldn’t do this without you.
Looking back over the past four years, Blu Genes has made great strides. We have partnered with two prominent North American research hospitals to propel research initiatives that offer real and tangible treatments for infants with Tay-Sachs disease.
We share this success with our donors who have made it possible.
In 2017, we embarked on a mission to launch a charitable foundation to specifically seek out and support critical research needed to save the lives of infants and children faced with rare genetic diseases. Blu Genes Foundation was created from a personal mission, as the granddaughter of our founders was diagnosed with Tay-Sachs disease, a rare and fatal genetic disorder for which there is no cure. Our founders discovered that great research is taking place globally for rare diseases like Tay-Sachs. However, they are seriously under funded and often stall due to financial hurdles.
Four years later, we continue to raise funds to advance gene therapy and strategically invest our resources in world-class research.
Our initial philanthropic investment was with the University of Massachusetts. It became the catalyst in advancing a decade of research for a gene therapy treatment for Tay-Sachs to the first in-human clinical trial of its kind in the world. This extraordinary achievement continues with the progressing trial and goal of treatment being available in the clinic within the near future.
Blu Genes has now joined with SickKids Hospital to launch a new gene editing research here in Toronto. This is a tremendous achievement as SickKids Research Institute is the largest Canadian hospital-based child health research institute and has the expertise and ability to translate ground-breaking research into in-clinic treatments. Dr. Zhenya Ivakine will focus his gene editing expertise on Tay-Sachs disease – working towards a treatment with curative potential. A collaboration with SickKids is a great honour, and we are excited for you to share in this success.
We are filled with hope as we move into a new season of opportunity in finding treatments for Tay-Sachs disease.
Thank you for being an important part of the Blu Genes Foundation’s success story.
Gianpiero Di Rocco