Blu Genes Foundation | Patient groups push abandoned rare disease gene therapy toward clinical trial | Left-to-right_-Teaghan-Duff-Talia-Duff-Jocelyn-Duff-and-John-Duff.-Courtesy-photo

Left-to-right_-Teaghan-Duff-Talia-Duff-Jocelyn-Duff-and-John-Duff.-Courtesy-photo

Published October 2, 2025 at 2400 × 1350 in Patient groups push abandoned rare disease gene therapy toward clinical trial