Published in Nature Medicine: Breakthrough gene therapy trial for Tay-Sachs Disease

Blu Genes Foundation supported: Duel-vector rAAVrh8 gene therapy for GM2 gangliosidosis: a phase I/II trial

Published in Nature Medicine: Groundbreaking Phase I/II Trial by Umass of Dual-Vector rAAVrh8 Gene Therapy for Tay-Sachs Disease, supported by Blu Genes